Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects

Muhammad  umair

doi:10.24911/JBCGenetics.183-1733834270

2024, Vol: 7, Issue: 2

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Editorial
Online Published: 21 Dec 2024

JBCGenetics. 0; 0(0):

doi: 10.24911/JBCGenetics.183-1733834270

Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects

Muhammad umair.

Abstract
The emergence of gene therapy has heralded a revolutionary era in the medical domain, especially for the treatment of rare genetic disorders. These conditions, stemming from mutations in individual genes, frequently result in severe health issues with few treatment options. For years, the outlook for individuals with inherited rare diseases was dire, as conventional therapies failed to address most of these disorders. However, recent progress in gene therapy is unlocking new possibilities for curing or alleviating the impact of these disorders by directly modifying the genetic material at the root of the disease. This editorial delves into the importance, constraints, and future prospects of gene therapy in the context of inherited rare diseases, highlighting its role as a pioneering force in personalized medical care.

Key words: Gene Therapy, Disease, Genetics, faulty gene, treatment

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Pubmed Style

umair M, . Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects. JBCGenetics. Online First: 21 Dec, 2024. doi:10.24911/JBCGenetics.183-1733834270

Web Style

umair M, . Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects. https://www.jbcgenetics.com/?mno=232368 [Access: December 22, 2024]. doi:10.24911/JBCGenetics.183-1733834270

AMA (American Medical Association) Style

umair M, . Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects. JBCGenetics. Online First: 21 Dec, 2024. doi:10.24911/JBCGenetics.183-1733834270

Vancouver/ICMJE Style

umair M, . Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects. JBCGenetics, [cited December 22, 2024]; Online First: 21 Dec, 2024. doi:10.24911/JBCGenetics.183-1733834270

Harvard Style

umair, M. & (0) Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects. JBCGenetics, Online First: 21 Dec, 2024. doi:10.24911/JBCGenetics.183-1733834270

Turabian Style

umair, Muhammad, and . 0. Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects. Journal of Biochemical and Clinical Genetics, Online First: 21 Dec, 2024. doi:10.24911/JBCGenetics.183-1733834270

Chicago Style

umair, Muhammad, and . "Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects." Journal of Biochemical and Clinical Genetics Online First: 21 Dec, 2024. doi:10.24911/JBCGenetics.183-1733834270

MLA (The Modern Language Association) Style

APA (American Psychological Association) Style

umair, M. & (0) Gene Therapy for Rare Genetic Disorders: Transformative Progress, Challenges, and Future Prospects. Journal of Biochemical and Clinical Genetics, Online First: 21 Dec, 2024. doi:10.24911/JBCGenetics.183-1733834270

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